Based in Dallas, Texas, AveXis is a clinic-stage gene therapy platform company establishing unique industry alliances to create innovative treatments for people with unmet medical needs. Spinal muscular atrophy (SMA) is the company's first focus.
Market
Gene Therapy
Location
Dallas,
Texas,
USA
Coinvestors
Adage Capital Management, Deerfield Management Company, L.P., Foresite Capital, Janus Capital, QVT Financial, RA Capital, Roche Venture Fund, Rock Springs Capital, RTW Investments, T. Rowe Price Associates, Venrock